US health agencies postpone rare diseases event
A two-day meeting aimed at raising awareness among policymakers and the public about rare diseases scheduled for the end of ...
US health agencies postpone rare disease day
A two-day meeting aimed at raising awareness among policymakers and the public about rare diseases, scheduled for the end of ...
‘That could be your family member’: Rare diseases affect 30 million Americans
The National Organization for Rare Disorders is a coalition of patient advocacy groups and the first national nonprofit that ...
Advocating for a child with a rare disorder brings heartbreak. And then there’s the joy.
When a child might not be — when something is wrong, yet no one seems to know what it is — the anxiety is soul-crushing. And ...
Rolling Out2d
7 rare diseases parents might pass to their children
From life-altering genetic conditions to promising new treatments, here's what you need to know about 7 inherited diseases ...
Innovations in research and treatment for rare diseases
More than 30 million people in the United States are affected by rare diseases, many of which are life-threatening conditions ...
Scientists Describe Rare Syndrome Following Covid Vaccinations
In a small study, patients with the syndrome were more likely to experience reactivation of Epstein-Barr virus and high ...
JD Supra3h
Navigating Key Challenges in M&A Deals in the Rare Disease Sector
In honor of Rare Disease Day on February 28, 2025, we will publish a series of posts throughout the month on As Prescribed ...
pharmaphorum1d
Paediatric rare diseases: Children are not small adults
Around 75% of rare diseases are diagnosed in childhood, with most before the age of two. With 30% of rare disease patients ...
Johns Hopkins Medicine4d
For Patients with Rare Diseases, Genetic Counselors Can Save Lives
As key members of the Johns Hopkins Department of Genetic Medicine, genetic counselors help patients with rare diseases ...
News Medical on MSN3d
Rare enterovirus strain in Spain raises alarms over potential outbreaks
Scientists in Spain detected Enterovirus C105 (EV-C105), a rare virus linked to respiratory and possible neurological illness ...