Given the rise in newborn screening for ALD since 2019, and the untapped potential of existing genetic research, the Halls ...

X-linked adrenoleukodystrophy (X-ALD) is a debilitating disease caused by mutations in the ABCD1 gene. Approximately 30% of affected boys develop the progressive ...

Market uncertainty makes investors nervous about investing in speculative industries. But Wall Street has high hopes for ...

Viking Therapeutics Inc (VKTX) reports significant R&D progress and financial bolstering despite increased losses and operational challenges.

A funny thing people do when you tell them a sad story is offer a consolation prize. There’s a special one for mothers mired ...

Since VKTX is devoid of marketed drugs, investors will focus on pipeline updates when it reports Q4 results next week.

With the Zynteglo approval in the bag, eyes now turn to bluebird's second gene therapy candidate elivaldogene autotemcel (eli-cel) for cerebral adrenoleukodystrophy (CALD), which has also been ...

Three people with a muscle-destroying disease destined to worsen got a little stronger when an implanted device zapped their ...

Julius Randle, who has been the Timberwolves' second leading scorer since coming to the team in an preseason trade, will be ...

Through messages, Paul had remained largely upbeat in the face of a terminal prognosis, showing us that he was still a ...