Two house cats died after contracting bird flu in the homes of dairy workers, a troubling sign that the virus may be moving between species and becoming more widespread. Most Read from BloombergTrump ...
BioMarin's gene therapy pipeline has had setbacks, including a three-year delay in US approval of Roctavian and stalled development of PKU gene therapy BMN 307 as the Food and Drug Administration ...
Under terms of the deal, Stoke will spearhead global development of zorevunersen, while Biogen will receive exclusive rights ...
Bengaluru: The Organization for Rare Diseases India (ORDI) announced the tenth edition of its annual awareness run, Racefor7, Sunday.
One expert who studies emerging infectious diseases called Kennedy's past tweets and remarks about the HPV vaccine "complete ...
For patients and caregivers living with rare diseases, life can be a daily struggle. Ahead of World Rare Disease Day this ...
When a child might not be — when something is wrong, yet no one seems to know what it is — the anxiety is soul-crushing. And ...
Ekho Studio completes 7,000 sq ft office design, bringing Alexion into the AstraZeneca fold at St Pancras Square, London ...
Ionis relies on upfront payments and licensing fees from partners, as well as Spinraza royalties, to drive revenue today, but its rapidly advancing portfolio should help diversify revenue. 2025 is ...
The evolution of cell and gene therapy is reshaping drug discovery, providing new hope for rare diseases and cancer through innovative gene editing approaches.
“The Tree Man was Dede Koswara, an Indonesian man who suffered from a rare genetic disorder called Epidermodysplasia ...
A gene variant identified in a family and studied in a fruit fly model may offer protection against a rare X-linked seizure ...
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