X-linked adrenoleukodystrophy (X-ALD) is a debilitating disease caused by mutations in the ABCD1 gene. Approximately 30% of affected boys develop the progressive ...

County Clerk Anthony Vega said turnout is generally lower in municipal elections a few months after a presidential contest, ...

Unless the two appeal the board’s ruling to judicial review in Lake County Circuit Court, Taylor remains on the ballot, which ...

Inspired by their 9-month old son William, who was diagnosed with ALD after a newborn screening, the Hall family seeks to jumpstart research into the rare disease, in partnership with The Dallas ...

It is either tragically funny or devastatingly sad that while a genetic counselor explained the random lunacy of my son’s ...

Bluebird bio could be just a few months away from approval of its gene therapy for rare disease cerebral adrenoleukodystrophy (CALD) in the EU, after the EMA started an accelerated review.

It is estimated that around a third of patients with ALD will go on to develop progressive ... of Harvard Medical School. In the US, a gene therapy for cALD from bluebird bio – Skysona (elivaldo ...

DURECT Corporation today announced the publication of a peer-reviewed article on the AHFIRM trial data in NEJM Evidence. The full article, entitled, "Larsucosterol for the Treatment of ...

Growth Drivers of The Gene Therapy Industry As per IMARC, the US gene therapy market size has been pegged at US$1,312.2 million in 2024. The market should reach US$3,697.8 million by 2033.