A new study in Human Gene Therapy describes a machine learning (ML) model that can be used as a surrogate for laborious in ...

Biotech firms are engineering smarter, safer gene delivery systems to enhance the safety and efficacy of genetic medicines.

Cross-species BBB-penetrant IV-delivered AAV gene therapy provides broad and robust CNS tau lowering in tauopathy mouse ...

Gene therapy represents one of the fastest growing biotherapeutics worldwide, with AAV at the forefront. This rapid growth is ...

8 Humoral and cellular responses to the AAV capsid and factor IX were measured periodically after treatment with the use of a neutralizing antibody assay and an interferon-γ enzyme-linked ...

“We believe STAC-BBB, our industry-leading intravenously delivered AAV capsid, has the potential to play an important role in the treatment landscape by addressing longstanding challenges ...

She will discuss how a new kit from Bio-Rad can simultaneously measure viral titer, capsid titer and empty–full ratio in AAV samples, empowering and improving gene therapy research.

Highly experienced in gene therapy dealmaking, Pettenaro will be driving Coave’s business development activities and ...

Agreement grants Lilly rights to employ Sangamo’s novel proprietary capsid, STAC-BBB, for up to five potential disease targets Sangamo to receive an $18 million upfront license fee and is ...