As scientists explore treating genetic disorders before birth, the promise of foetal gene therapy is growing—but there are ...

In patients with mesenteric artery disease, they can experience weight loss and severe abdominal pain when they eat. These patients can also experience other symptoms including vomiting, dizziness, ...

In individuals with SMA type 1, this typically leads to symptoms within the first six months of life, and without treatment, they are likely to die before the age of two. While there’s currently ...

Researchers expected counselors working with some populations to report barriers with SMA screening, but all counselors faced ...

Liver damage related to Zolgensma gene therapy usually resolves within a few months of treatment, a study found.

and improving the overall quality of life for those affected by SMA. The combination of physical therapy, nutrition, and emotional support does not just treat symptoms; it provides the patients ...