Alexa Beichler's boys were born with classic phenylketonuria (PKU), a metabolic condition that requires them to be on medical-grade formula for life Anya Leon is a Senior News Editor and the ...

"The addition of Jnana's drug discovery technology and small molecule pipeline in PKU and autoimmune diseases will strengthen our R&D in the Boston area of the US, one of the most important ...

Each enzyme molecule has a special place called the active site where ... One example is phenylketonuria (or PKU), a rare inherited disease where the body lacks the enzyme to process proteins. Because ...

Pegvaliase statistically significantly lowered blood Phe levels in adolescents with PKU compared with diet alone. Topline data were announced from a phase 3 trial evaluating pegvaliase-pqpz in ...

Single-molecule technologies have enabled us to explain ... A healthy and fluid ecosystem is needed for translational research, and at PKU, we have abundant resources and strengths in a variety ...

MZE829 Phase 2 HORIZON Trial Enrolling Patients with APOL1 Kidney Disease (AKD); Initial Data Expected in Q1 2026MZE782 Phase 1 Healthy Volunteer ...

From single-molecule imaging to next-generation sequencing ... BIOPIC, a technology-driven biomedical research centre at PKU is dedicated to both developing and applying the most advanced ...

MZE782 in CKD and PKU MZE782 is an oral small molecule targeting the solute transporter SLC6A19, with potential to be a first-in-class treatment for approximately five million U.S. patients with ...