New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing ...
DMD is much more common in males, affecting an estimated 14 in 100,000 males ages 5 to 24 years in the United States. It‘s considered relatively rare in females. Symptoms of DMD usually begin ...
The patient, whom Sarepta described as a young man and later told news outlets was 16 years old, suffered acute liver failure ...
Delandistrogene moxeparvovec, a gene therapy approved for the treatment of Duchenne muscular dystrophy (DMD), was found ...
Multiparametric quantitative MRI could potentially help differentiate between Duchenne muscular dystrophy and Becker muscular ...
RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, ...
Long-term treatment with Duvyzat (givinostat) may help delay the loss of walking ability and lessen the decline in lung ...
New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing ...
DMD, a genetic disorder affecting 1 in 5000 ... potentially worsening cognitive symptoms. The cerebellum, vital for motor learning, but also language and higher cognitive functions, is affected ...
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