Scientists from The Hospital for Sick Children (SickKids) and University of Las Vegas Nevada (UNLV) have uncovered a genetic link between autism spectrum disorder (ASD) and a rare genetic condition ...

DM1 is an inherited condition which causes progressive muscle loss and weakness. While ASD is present in around 1% of the general population, it is 14 times more likely to develop in people with DM1.

RBC noted that while Avidity (RNA) is ahead on myotonic dystrophy type 1, or DM1, Dyne (DYN) may catch up with its Fab-ASO ...

In recent years, a growing understanding of myotonic dystrophy type 1 (DM1)—an often fatal, devastating, rare neuromuscular disorder that causes muscle weakness and other life-limiting ...

DM1 is an inherited condition which causes progressive muscle loss and weakness. While ASD is present in around one per cent of the general population, it is 14 times more likely to develop in ...

Del-desiran is the first investigational treatment for DM1 to receive Orphan Drug designation in Japan. Del-desiran has also received Breakthrough Therapy, Orphan Drug and Fast Track designations ...

This marks the first such designation for a DM1 treatment in Japan and follows similar recognitions in the U.S. and Europe. According to InvestingPro data, the company maintains a strong financial ...

The team showed that the genetic variation that causes DM1—tandem repeat expansions (TREs) in the DMPK gene—also impacts brain development. The combined results of their research, including ...