Autism may be caused by a little-known genetic condition, experts say. They've found children with myotonic dystrophy type 1 ...

Scientists from The Hospital for Sick Children (SickKids) and the University of Las Vegas, Nevada (UNLV) have uncovered a ...

A rare disorder called myotonic dystrophy type 1 (DM1) causes weakness and muscle loss that gets progressively worse... | ...

Scientists found a genetic link between autism and DM1, where repeat DNA sequences disrupt brain gene splicing. This sheds light on ASD’s development and opens new paths for targeted treatments.

Researchers suggest discovery of genetic link between ASD and DM1 opens up potential new therapeutic avenues for ASD.

Del-desiran is the first investigational treatment for DM1 to receive Orphan Drug designation in Japan. Del-desiran has also received Breakthrough Therapy, Orphan Drug and Fast Track designations ...

New research has uncovered a genetic connection between autism spectrum disorder (ASD) and myotonic dystrophy type 1 (DM1), a rare neuromuscular disease.

In recent years, a growing understanding of myotonic dystrophy type 1 (DM1)—an often fatal, devastating, rare neuromuscular disorder that causes muscle weakness and other life-limiting ...

Highlighted by Genentech's recent US regulatory submission for trastuzumab–DM1, antibody–drug conjugation technology could be heading for the mainstream in anticancer drug development.

This marks the first such designation for a DM1 treatment in Japan and follows similar recognitions in the U.S. and Europe. According to InvestingPro data, the company maintains a strong financial ...

DM1 is an inherited condition which causes progressive muscle loss and weakness. While ASD is present in around one per cent of the general population, it is 14 times more likely to develop in ...