Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

Every living creature on Earth needs to protect itself from things that would do it harm. Bacteria are no different. And ...

One of the most commonly used gene-delivery methods relies on engineered viruses to insert stretches of genetic material into ...

In a world first, scientists used CRISPR to fix a baby's unique genetic mutation. The report offers hope for personalized ...

Drug development takes years, time KJ did not have. But his doctor, Rebecca Ahrens-Nicklas, a metabolic-disease expert at the ...

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

Learn more about whether BioCryst Pharmaceuticals, Inc. or CRISPR Therapeutics AG is a better investment based on AAII's A+ ...

PHILADELPHIA (WPVI) -- An infant, who was born with a deadly disease, is now thriving, thanks to a medical first performed at the Children's Hospital of Philadelphia. KJ Muldoon, of Clifton Heights, ...