The cell and gene therapy space in recent months has hit several speedbumps, including layoffs, dropped drugs and ...

At Jichi Medical University, in Tochigi, north of Tokyo, much research has focused on establishing the safety and long-term efficacy of AAV vector-mediated gene therapies, including navigating ...

Amid a reckoning for the gene therapy field, Vertex Pharmaceuticals has joined a growing list of companies paring back their research efforts around the adeno-associated virus (AAV) vectors used to | ...

First, the researchers developed an AAV (AAV-Sia6e) that can deliver genome editing tools to a wide range of inner ear cells that form gap junctions. AAV is a useful vector for delivering genes ...

ReGenX's AAV Vector Technology gives extremely efficient and stable gene expression in neonatal and adult animals, and can be used to create disease models and to study gene function and target ...

Age-related macular degeneration (AMD) is the leading cause of blindness among older adults. The exudative or ‘wet’ form of the disease is characterized by the growth of abnormal blood vessels from ...

Siren said proceeds will go toward investigational new drug (IND)-enabling animal studies and clinical-grade production of ...

Discover the advantages of Minicircles in AAV vector manufacturing. Demonstrate how capillary electrophoresis (CE) helps ensure the quality of Minicircle DNA. Webinars will be available for unlimited ...